Sem | Biomedical Scientist on Instagram: "If a virus hijacks cells to deliver genetic material, what happens when scientists control what it delivers? That logic led to viral gene therapy. Luxturna became the first FDA approved in vivo viral gene therapy for an inherited disease in 2017. It uses an engineered adeno-associated virus (AAV) to deliver a working RPE65 gene to retinal cells in biallelic RPE65 related inherited retinal disease. A one time treatment per eye can restore light sensitivit